87. Garcia-Lopez et al., Nature Communications (2018)

“Targeting RNA structure in SMN2 reverses spinal muscular atrophy molecular phenotypes”.

      Garcia-Lopez A, Tessaro F, Jonker HRA, Wacker A, Richter C, Comte A, Berntenis N, Schmucki R, Hatje K, Petermann O, Chiriano G, Perozzo R, Sciarra D, Konieczny P, Faustino I, Fournet G, Orozco M, Artero R, Metzger F, Ebeling M, Goekjian P, Joseph B, Schwalbe H, Scapozza L.
      Nat Commun. 2018 May 23;9(1):2032. doi: 10.1038/s41467-018-04110-1.